Thanks to Ali Sadeghi-Khomami, PhD, PBI research scientist, for the following heads-up: On Friday, March 28, 2025, Sanofi Inc. announced the much-awaited approval of fitusiran (Qfitlia®), a “rebalancing” therapeutic that dramatically reduces the ABR in hemophilia A and hemophilia B patients ≥12 YOA with or without inhibitors. Fitusiran is a messenger RNA inhibitor (RNAi) that … Continue reading Fitusiran Approved March 28, 2025